Found 14 matching trials
Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
PHASE2The purpose of this study is to evaluate the effects of EPI-743 in children...
Location
Stanford University
A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia
PHASE2The primary objective of the study is to assess the pharmacokinetics (PK) a...
Location
The Children's Hospital of Philadelphia
Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome
PHASE2EPI-743 in Leigh syndrome participants that participated in previous EPI743...
A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsy
PHASE2This is a parallel-arm, double-blind, placebo-controlled study with a scree...
Location
University of California
Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)
PHASE3The purpose of this study is to confirm the treatment effects of vatiquinon...
Location
University of California Los Angeles
Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia
PHASE2The purpose of this study is to examine the effects of EPI-743 on visual fu...
Location
University of California Los Angeles
EPI-743 for Metabolism or Mitochondrial Disorders
PHASE1Background:
* Mitochondria are the parts of cells that help produce energy...
Location
National Institutes of Health Clinical Center, 9000 Rockville Pike
EPI-743 for Mitochondrial Respiratory Chain Diseases
N/AThis study will evaluate the safety and efficacy of EPI-743 in participants...
Status
No Longer Available
An Exploratory Open Label Study of EPI-743 (Vincerinone TM) in Children With Autism Spectrum Disorder
PHASE2The investigators hypothesize that EPI-743 may provide clinical benefit to ...
Location
Multiple Locations
EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment
PHASE2The aim of the research is to investigate the safety and efficacy of EPI-74...
Location
Bambino Gesù Hospital and Research Institute